Scientific and Clinical Hub for Orphan Drug Development

With rapid and cost-effective genome sequencing becoming the norm, many causal mutations for inherited genetic diseases are being rapidly determined. The discovery of new genes for inherited diseases is enabling rapid genetic and chemical genetic platforms to be used to discover drug targets and drugs/drug-like molecules as potential treatment options for patients with inherited diseases. This project is focusing on the identification of compounds that could potentially treat human genetic diseases, with a focus on childhood blinding disorders, and muscular dystrophies – the expertise of the industrial partner AGADA Biosciences. The research will identify novel drugs/drug-like molecules for the treatment of patients suffering from these inherited diseases.

Faculty Supervisor:

Christopher McMaster

Student:

Partner:

AGADA Biosciences

Discipline:

Life Sciences

Sector:

Professional, scientific and technical services

University:

Dalhousie University

Program: