Drug Repurposing for Neuromuscular Diseases

SMA is a neurodegenerative disease characterised by the loss of lower motor neurons and is an incurable disease. SMA is the leading genetic cause of early childhood lethality, with an incidence of 1 in 6,000 to 10,000 live births and a carrier frequency of 1 in 35-40. Current therapeutic strategies under development are almost exclusively […]

Read More